Scientists at UMass Medical School have developed a strategy for editing and repairing a particular type of genetic mutation associated with microduplications using CRISPR/Cas9 and a seldom-used DNA ...

A new study describes a base editing method for treating spinal muscular atrophy (SMA). This supports early signs that “single-shot” treatments from clinical trials using genome editing technologies ...

Base editing—the genome editing technique that alters base pairs using a nuclease-deficient Cas9 fused to a deaminase—was found to restart fetal hemoglobin expression in sickle cell disease (SCD) ...

A permanent cure for HIV infection remains elusive due to the virus's ability to hide away in latent reservoirs. But now, scientists show that they can excise HIV DNA from the genomes of living ...

Want to keep the riffraff out of the gene pool party? Sneak in and slam the gate before they arrive. That’s the central idea of a new strategy by Rice University scientists who seek to avoid ...

Professor Saar Gill and Professor Carl June from the Perelman School of Medicine at the University of Pennsylvania published a research paper titled: Epitope base editing CD45 in hematopoietic cells ...

This study examined the efficacy of the EDIT Strategy on proofreading skills of postsecondary individuals who attended a campus-based college program for students with developmental disabilities. A ...